Original ArticleNeurological Dysfunction in Early Maturity of a Model for Niemann–Pick C1 Carrier Status
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Keywords
NPC1
Niemann–Pick disease type C
haploinsufficiency
Carrier
Heterozygote disease
Neurological
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Copyright © 2016 The American Society for Experimental NeuroTherapeutics, Inc. Published by Elsevier B.V. All rights reserved.